Browsing Tag
Ifezuntirgene Inilparvovec
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uniQure shares tumble as Huntington’s gene therapy shows weaker four-year cUHDRS benefit
uniQure shares plunge as four-year ifezuntirgene data show mixed Huntington’s results while the gene therapy awaits FDA review.
uniQure files AMT-130 in U.S. and U.K. as Huntington’s gene therapy reaches regulators
uniQure has submitted AMT-130 for accelerated U.S. approval and filed simultaneously in the United Kingdom, moving the Huntington’s gene therapy from regulatory planning into formal review.