Browsing Tag
RNAi
4 posts
From rare disease to mass market: plozasiran gets FDA green light for severe hypertriglyceridemia review
Arrowhead’s plozasiran receives FDA Breakthrough Therapy status for severe hypertriglyceridemia. Learn what this means for trials, patients, and the RNAi market.
December 2, 2025
How Arrowhead Pharmaceuticals’ first FDA-approved drug Redemplo could reshape treatment for familial chylomicronemia syndrome
Discover how Arrowhead Pharmaceuticals’ FDA approval for Redemplo could transform care for familial chylomicronemia syndrome.
November 18, 2025
Can Alnylam Pharmaceuticals’ vutrisiran reverse cardiac damage? HELIOS-B Phase 3 ATTR-CM trial says yes
New HELIOS-B data shows vutrisiran improves cardiac structure and kidney outcomes in ATTR-CM. Find out how Alnylam’s RNAi drug is reshaping treatment.
November 9, 2025
Biotech rivals clash as Arrowhead sues Ionis over RNA-based triglyceride therapy
Arrowhead sues Ionis over APOC3 patent dispute as plozasiran nears FDA approval. Discover what’s at stake in this RNA-based biotech rivalry.
September 11, 2025