Browsing Tag
Phenylketonuria
7 posts
BioMarin Pharmaceutical (Nasdaq: BMRN) secures FDA approval to expand PALYNZIQ use in adolescents with phenylketonuria
Find out how BioMarin Pharmaceutical Inc.’s FDA approval for adolescent PALYNZIQ use could reshape PKU treatment and long-term disease control.
FDA grants priority review for BioMarin’s PALYNZIQ to treat adolescents with phenylketonuria (PKU)
Find out how BioMarin’s PALYNZIQ priority review could transform PKU treatment for adolescents and reshape the company’s rare-disease strategy.
What your urine says about your health: The science behind urinalysis explained
Explore how urinalysis helps detect kidney, liver, and metabolic disorders through simple tests of urine colour, pH, protein, and more.
BioMarin shares rise as new VOXZOGO and PALYNZIQ data reinforce market potential
Discover how BioMarin’s latest clinical data on VOXZOGO and PALYNZIQ at ACMG 2025 offers promising insights into rare disease treatments and what it means for the market.
FDA accepts PTC Therapeutics’ NDA for Sepiapterin, aiming for breakthrough in PKU treatment
PTC Therapeutics, Inc. has announced a significant step forward in its mission to combat phenylketonuria (PKU) by receiving…
Dr. Reddy’s Laboratories launches Sapropterin dihydrochloride powder in US
Dr. Reddy’s Laboratories has launched Sapropterin Dihydrochloride Powder for Oral Solution, 100mg, a generic of BioMarin’s Kuvan (sapropterin…
Dr. Reddy’s launches Sapropterin Dihydrochloride Tablets generic version in US
Indian pharma company Dr. Reddy’s Laboratories has launched a generic version of phenylalanine hydroxylase activator Sapropterin Dihydrochloride Tablets,…