FDA committee endorses Zevra Therapeutics’ arimoclomol as a treatment for Niemann-Pick Disease Type C

Pallavi Madhiraju- August 3, 2024 0

In a notable advancement for rare disease treatment, Zevra Therapeutics, Inc. (NasdaqGS: ZVRA) has received a significant endorsement from the U.S. Food and Drug Administration ... Read More

Vertex Pharmaceuticals’ suzetrigine approved for FDA review: A breakthrough in pain management

Pallavi Madhiraju- July 30, 2024 0

Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) has announced a pivotal advancement in the treatment of acute pain. The U.S. Food and Drug Administration (FDA) has officially ... Read More