Browsing Tag
Danon disease
2 posts
Why Rocket Pharmaceuticals shareholders are filing suit over adverse event risks in RP-A501
A class action lawsuit claims Rocket Pharmaceuticals misled investors about the safety and effectiveness of its gene therapy. Find out what’s at stake.
IPS HEART gets third FDA pediatric rare disease designation for ISX9-CPC
IPS HEART, a private cell therapy company developing treatments for Duchenne muscular dystrophy and heart failure, announced that…