FDA approves Vertex and CRISPR Therapeutics’ CASGEVY for sickle cell disease
Vertex Pharmaceuticals Incorporated and CRISPR Therapeutics have announced a significant milestone in medical science with the U.S. Food and Drug Administration’s (FDA) approval of CASGEVY (exagamglogene autotemcel [exa-cel]), a revolutionary CRISPR/Cas9 genome-edited cell therapy. This approval marks a significant advancement in the treatment of sickle cell disease (SCD) for patients aged 12 and older experiencing […]