Browsing Tag
AAV vector
3 posts
Why the FDA’s warning on Elevidys matters for Duchenne muscular dystrophy treatment
Sarepta’s Elevidys gene therapy now carries an FDA boxed warning. Find out what it means for Duchenne patients, investors, and gene therapy safety.
Genethon and Atamyo expand gene therapy pipeline with key trial milestones and global collaboration momentum
Genethon and Atamyo Therapeutics progress gene therapy trials for Duchenne and LGMD, while France’s GenoTher Biocluster strengthens global biotech alliances.
Biogen to acquire Nightstar Therapeutics in a deal worth $800m to target retinal diseases
In a significant move within the biotech sector, Biogen, the US-based biotechnology giant, has announced its agreement to…